

Indication | MeSH | Ontology | ICD-10 | Ph 1 | Ph 2 | Ph 3 | Ph 4 | Other | Total |
|---|---|---|---|---|---|---|---|---|---|
| Mucopolysaccharidoses | D009083 | — | E76.3 | 3 | 4 | 3 | 1 | — | 8 |
| Syndrome | D013577 | — | — | 1 | 2 | — | 1 | — | 3 |
| Mucopolysaccharidosis vi | D009087 | — | — | — | — | 1 | 1 | — | 2 |
Indication | MeSH | Ontology | ICD-10 | Ph 1 | Ph 2 | Ph 3 | Ph 4 | Other | Total |
|---|---|---|---|---|---|---|---|---|---|
| Mucopolysaccharidosis iii | D009084 | — | E76.22 | 4 | 6 | 1 | — | — | 7 |
| Mucopolysaccharidosis ii | D016532 | — | E76.1 | 2 | 2 | 2 | — | — | 4 |
| Mucopolysaccharidosis iv | D009085 | — | E76.210 | — | — | 2 | — | 1 | 3 |
| Sudden infant death | D013398 | — | — | — | — | 1 | — | — | 1 |
Indication | MeSH | Ontology | ICD-10 | Ph 1 | Ph 2 | Ph 3 | Ph 4 | Other | Total |
|---|---|---|---|---|---|---|---|---|---|
| Metachromatic leukodystrophy | D007966 | — | E75.25 | 4 | 6 | — | — | — | 7 |
| Mucopolysaccharidosis i | D008059 | — | E76.0 | 1 | 2 | — | — | — | 2 |
| Drug common name | Cebsulfase alfa |
| INN | — |
| Description | — |
| Classification | Unknown |
| Drug class | — |
| Image (chem structure or protein) | ![]() |
| Structure (InChI/SMILES or Protein Sequence) | — |
| PDB | — |
| CAS-ID | — |
| RxCUI | — |
| ChEMBL ID | — |
| ChEBI ID | — |
| PubChem CID | — |
| DrugBank | — |
| UNII ID | — |